Development of a human hematopoietic stem cell targeted platform through multiplexed targeting and de-targeting modifications of a common viral gene transfer vector for safe and effective editing of stem cell compartment in vivo.

Authors

Dmitry Shayakhmetov, Emory University, USAFollow
Jia Yao, Emory University, Atlanta, USA
Svetlana Atasheva, Emory University, Atlanta, USA
Nelson C. Di Paolo, AdCure Bio, Atlanta, USA
Nicole Wagner, Case Western Reserve University, Cleveland, USA
Phoebe L. Stewart, Case Western Reserve University, Cleveland, USA

Conference Dates

April 4 - 8, 2024

Abstract

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Recommended Citation

Dmitry Shayakhmetov, Jia Yao, Svetlana Atasheva, Nelson C. Di Paolo, Nicole Wagner, and Phoebe L. Stewart, "Development of a human hematopoietic stem cell targeted platform through multiplexed targeting and de-targeting modifications of a common viral gene transfer vector for safe and effective editing of stem cell compartment in vivo." in "Delivery Of Nucleic Acid Therapeutics II: Biology, Engineering And Development", Steven F. Dowdy, UCSD School of Medicine, USA; Laura Sepp-Lorenzino, Intellia Therapeutics, USA; Matt Stanton, Generation Bio, USA Eds, ECI Symposium Series, (2024). https://dc.engconfintl.org/nucleic_acid_therapeutics_ii/17