A nonviral CRISPR platform for in vivo retinal gene editing: Manufacturing and analytical considerations
Conference Dates
February 1 – 5, 2026
Abstract
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Recommended Citation
Apoorva Ramamurthy, Krishanu Saha, Shaoqin Gong, T. Michael Nork, William Murphy, Kelly Ormond, Bikash R. Pattnaik, Melissa Skala, Shengdar Tsai, Jonathan Watts, Ruixuan Gao, Meha Kabra, Varun Katta, Garret Manquen, John Krutty, Marcela Tabima, Srikumar Sengupta, Pawan Shahi, Nicholas Shinners, Divya Sinha, Piper Rawding, Atish Wagh, Alex Xie, Min Zhu, Song Zhang, and Zhanpeng Zhang, "A nonviral CRISPR platform for in vivo retinal gene editing: Manufacturing and analytical considerations" in "Advancing Manufacture of Cell and Gene Therapies IX", John Moscariello, Neuvogen, USA Corinne Hoesli, McGill University, Canada Bruno Marques, Century Therapeutics, USA Eds, ECI Symposium Series, (2026). https://dc.engconfintl.org/cell_gene_therapies_ix/56